Orphan Drugs
2026-07-12 · Department of Health and Social Care · HL2000 · Official question
Question
To ask His Majesty's Government what assessment they have made of the impact of the 2025 Highly Specialised Technologies routing criteria updates on the number of orphan medicines being diverted to the Standard Technology Appraisal (STA) pathway; and what
Answer
The National Institute for Health and Care Excellence (NICE) highly specialised technologies programme (HST) is reserved for the evaluation of a small number of medicines licensed for the treatment of very rare, very severe diseases. Decisions on whether ...