Metachromatic Leukodystrophy
Commons · Question 5801 · Tabled 1 Jun 2026 · Department of Health and Social Care · Official record
Answered 9 Jun 2026
Question
Asked by Gregory Stafford
To ask the Secretary of State for Health and Social Care, how many children diagnosed with metachromatic leukodystrophy since the approval of gene therapy treatment have been assessed as ineligible for treatment because diagnosis occurred after symptoms d
Answer
Answered by Preet Kaur Gill, 9 Jun 2026
Libmeldy, the gene therapy treatment for metachromatic leukodystrophy (MLD) has been funded nationally by NHS England since 2022 and is delivered exclusively through the specialist children’s service at Royal Manchester Children’s Hospital. Information on...