Rare Diseases: Gene Therapies
Commons · Question 103088 · Tabled 5 Jan 2026 · Department of Health and Social Care · Official record
Answered 12 Jan 2026
Question
Asked by Freddie van Mierlo
To ask the Secretary of State for Health and Social Care, what steps he is taking to support the development of gene therapy treatments for rare genetic diseases such as tyrosinemia and Gaucher disease.
Answer
Answered by Zubir Ahmed, 12 Jan 2026
The Government is committed to improving the lives of those living with rare diseases, such as tyrosinemia and Gaucher disease. Through the UK Rare Diseases Framework, the Government supports access to specialist care, treatment, and drugs as a priority. ...