Written questions

Vamorolone

Commons · Question 62450 · Tabled 24 Jun 2025 · Department of Health and Social Care · Official record

Answered 30 Jun 2025

Question

Asked by Freddie van Mierlo

To ask the Secretary of State for Health and Social Care, how many patients have accessed Vamorolone since it was given NICE approval for Duchenne Muscular Dystrophy; what assessment he has made of the adequacy of availability of Vamorolone to patients wi

Answer

Answered by Karin Smyth, 30 Jun 2025

The National Institute for Health and Care Excellence (NICE) published its technology appraisal, titled Vamorolone for treating Duchenne muscular dystrophy in people 4 years and over, on 16 January 2025. NHS England routinely commissioned vamorolone in li...